Functionalized linear poly(amidoamine)s are efficient vectors for intracellular protein delivery

Coue, G; Engbersen, JFJ

HERO ID

1461794

Reference Type

Journal Article

Year

2011

Language

English

PMID

21277918

HERO ID 1461794
In Press No
Year 2011
Title Functionalized linear poly(amidoamine)s are efficient vectors for intracellular protein delivery
Authors Coue, G; Engbersen, JFJ
Journal Journal of Controlled Release
Volume 152
Issue 1
Page Numbers 90-98
Abstract An effective intracellular protein delivery system was developed based on functionalized linear poly(amidoamine)s (PAAs) that form self-assembled cationic nanocomplexes with oppositely charged proteins. Three differently functionalized PAAs were synthesized, two of these having repetitive disulfide bonds in the main chain, by Michael-type polyaddition of 4-amino-1-butanol (ABOL) to cystamine bisacrylamide (CBA), histamine (HIS) to CBA, and ABOL to bis(acryloyl)piperazine (BAP). These water-soluble PAAs efficiently condense β-galactosidase by self-assembly into nanoscaled and positively-charged complexes. Stable under neutral extracellular conditions, the disulfide-containing nanocomplexes rapidly destabilized in a reductive intracellular environment. Cell-internalization and cytotoxicity experiments showed that the PAA-based nanocomplexes were essentially non-toxic. β-Galactosidase was successfully internalized into cells, with up to 94% of the cells showing β-galactosidase activity, whereas the enzyme alone was not taken up by the cells. The results indicate that these poly(amidoamine)s have excellent properties as highly potent and non-toxic intracellular protein carriers, which should create opportunities for novel applications in protein delivery.
Doi 10.1016/j.jconrel.2011.01.023
Pmid 21277918
Wosid WOS:000292718200012
Is Certified Translation No
Dupe Override No
Comments Source: Web of Science WOS:000292718200012
Is Public Yes
Language Text English
Keyword Bioreducible polymers; Disulfide reduction; Intracellular protein delivery; Poly(amidoamine); Polyelectrolyte complex